Duchenne muscular dystrophy (DMD) is characterized as a progressive weakness of muscles along with a shortened life span. As of today, there is no successful treatment. DMD is an inherited disease found on the X sex chromosome. Recently, a study demonstrated editing of the mice germline, using CRISPR/Cas9, to correct the dystrophin gene (Dmd) mutation. After monitoring muscle structure and function animals showed “2 to 100% correction of the Dmd gene”. The results reflected effective regeneration of muscle of the corrected cells, which gives hope that this could be a new treatment for disease-causing mutations in muscle cells for patients suffering by DMD.
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